We Are Genetic Navigators bringing together passionate, creative and dedicated professionals to join a rapidly growing biotech in our mission to translate novel genetic insights into lifesaving medicines.We are seeking an energetic, detail-oriented life-science focused college student who is motivated by the goal of improving the lives of patients through research, discovery and teamwork. The intern will be focused on Maze’s lead program, a small molecule investigational therapy for Pompe disease, which is currently in Phase 1 clinical evaluation. In addition to joining the development team in reviewing ongoing trial data, interacting with patient advocacy groups, and planning for an upcoming global phase 2 study, the intern will also have a research project involving review of the scientific rationale, clinical needs, epidemiology, potential regulatory path, and potential clinical development path for our investigational therapy in other glycogen storage diseases. This project will involve independent literature review and database searches that will be supplemented with regular discussions with key development functional leaders such as Maze’s head of regulatory affairs, clinical operations, translational biology, project management, and manufacturing to ensure successful completion. The intern will also participate in special activities with other interns from medicinal chemistry, computational biology, and human genetics.The summer intern will be overseen by the Chief Medical officer and the clinical development leadership team.Responsibilities:Supporting the clinical development team during the conduct of a phase 1 healthy volunteer study of a compound intended for use in Pompe disease, a rare glycogen storage diseaseResearching new clinical indications for an oral glycogen synthase 1 (GYS1) inhibitorPresenting findings to the Pompe disease/GYS1 core teamQualifications:Currently enrolled in a 4-year college or university with a major or strong interest in the life sciencesInterest in the biotech industry, specifically a small, fast-paced start-up environmentSelf-motivated, able to perform independent research and present findingsComfortable with basic functions involving power point, excel, and Microsoft wordTeam player, willing to learn new skills and take on additional clinical-oriented tasks as they arise